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Limb-Girdle muscular dystrophy

LGMD is a group of disorders with many subtypes caused by mutations in genes that affect the strength and function of the muscles around the hip and shoulder

Prevalence

1-9 / 100 000

3,310-29,790

US Estimated

5,135-46,215

Europe Estimated

Age of Onset

ICD-10

G71.0

Inheritance

Autosomal dominant

Autosomal recessive

Mitochondrial/Multigenic

X-linked dominant

X-linked recessive

5 Facts you should know

FACT

1

Limb-girdle muscular dystrophy is characterized by atrophy and weakness of the voluntary muscles of the hip and shoulder areas, i.e., “the limb-girdle area”

 

FACT

2

In the early stages of limb-girdle muscular dystrophy, affected individuals may have an unusual walking gait, such as waddling or walking on the balls of their feet, and may also have difficulty running

 

FACT

3

Muscle wasting may cause changes in posture or in the appearance of the shoulder, back, and arm

 

FACT

4

There is a wide disparity in how the condition evolves, it can be mild and slowly progressive or rapidly progressive

 

FACT

5

There are at least 20 different types of limb-girdle muscular dystrophy

 

Limb-Girdle muscular dystrophy is also known as...

Limb-Girdle muscular dystrophy is also known as:

  • Erb's muscular dystrophy
  • LGMD
 
 
 

What’s your Rare IQ?

Limb-girdle muscular dystrophy is also known as __________?
 

Common signs & symptoms

Shoulder Weakness

Weakness in the muscles around the shoulders can lead to difficulty lifting the arms overhead or performing activities that involve raising the arms

Gait Abnormalities

Individuals with LGMD may exhibit changes in their gait, such as waddling or walking on the toes, due to muscle weakness and imbalance

Falling

Muscle weakness and instability can increase the risk of falls, especially when walking on uneven surfaces or navigating stairs

Muscle Wasting (Atrophy)

Progressive muscle wasting or atrophy may occur as the disease advances, leading to a loss of muscle mass in affected areas

Pseudohypertrophy

Some forms of LGMD may be associated with pseudohypertrophy, where certain muscles appear enlarged due to fatty or connective tissue infiltration, masking underlying muscle wasting

Current treatments

Treatment for Von Hippel-Lindau (VHL) disease depends on the location and size of tumors. In general, the goal is to treat growths when they cause symptoms but are still small so they don't cause permanent damage. Treatment usually involves: 

Orthopedic Interventions

Orthopedic interventions, such as bracing or orthotic devices, may be used to provide support and stability to weakened muscles and joints, reduce the risk of falls, and improve mobility

Medications

While there are no specific medications to treat LGMD itself, certain medications may be prescribed to manage symptoms or complications associated with the condition. For example, medications may be used to alleviate muscle pain, reduce inflammation, or manage cardiac symptoms in individuals with LGMD

Top Clinical Trials

Top Treatments in Research